Patients Have Power!
Researching Treatment for an Ultra-Rare Disease
- Autor: Vários
- Narrador: Vários
- Editor: Podcast
- Duración: 0:17:01
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Sinopsis
Aaron interviews Dr. Alex Solyom, senior medical director at Enzyvant, about his team's work in developing a new therapy for an ultra-rare genetic condition known as Farber disease.